Despite a virtual conference due to COVID-19, the following research by Endpoint Outcomes and its clients will be published on the conference website.

  • Development of a Pediatric Faces Scale for use in Multiple Disease Areas
  • The Humanistic Burden of Glycogen Storage Disease Type Ia: The Impact on Symptoms, Diet, and Health-related Quality of Life
  • Development of Conceptual Frameworks and Pilot PRO Measures in OTC Deficiency
  • Development of Illustrations for Use in Pediatric Qualitative Interviews
  • Itch Reported Outcome Tool For Caregivers Of Pediatric Patients With Cholestatic Liver Disease: An Analysis Of Validation And Scoring From The ICONIC Maralixibat Study
  • A descriptive framework for understanding patterns of in intensive longitudinal patient diaries